Browsing Archive: September, 2011

Make Mine Rare

Posted by Fridrik Fridriksson on Wednesday, September 14, 2011,
With mounting interest from biotechs, Big Pharma, and the federal government, research on rare diseases is burgeoning.

http://the-scientist.com/2011/08/01/make-mine-rare/
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Reynt að nota Desipramine chlorhydrate við meðferð á Rett Syndrome

Posted by Fridrik Fridriksson on Wednesday, September 14, 2011,
On 12 June 2009, orphan designation (EU/3/09/643) was granted by the European Commission to Targeon SAS, France, for desipramine chlorhydrate for the treatment of Rett syndrome.

Desipramine chlorhydrate has been used in the treatment of depression since the 1960s. In Rett syndrome, the medicine is expected to treat breathing problems.

Girls with Rett syndrome tend to have low levels of norepinephrine, a substance in the brain and spinal cord that helps maintain a normal breathing rhythm. Desipr...
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Making connections

Posted by Fridrik Fridriksson on Monday, September 12, 2011,
Making connections.
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Can Rett Syndrome be reversed?

Posted by Fridrik Fridriksson on Monday, September 12, 2011,

Can Rett Syndrome be reversed?


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